Non-transfusion dependent thalassemia
Showing 1 - 25 of >10,000
Transfusion-dependent Thalassemia, Non-transfusion-dependent Thalassemia Trial in Worldwide (Deferasirox dispersable tablet
Completed
- Transfusion-dependent Thalassemia
- Non-transfusion-dependent Thalassemia
- Deferasirox dispersable tablet (DT)
- Deferasirox film coated tablet (FCT)
-
Alexandria, Egypt
- +16 more
Sep 6, 2021
Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))
Active, not recruiting
- Thalassemia
- Luspatercept
- +2 more
-
Los Angeles, California
- +16 more
Aug 16, 2022
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)
Recruiting
- Transfusion-dependent Thalassemia
- Thalidomide Capsules
- Placebo
-
Dhaka, BangladeshBangabandhu Sheikh Mujib Medical University
Oct 18, 2023
Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)
Active, not recruiting
- Beta Thalassemia Intermedia
-
Camperdown, New South Wales, Australia
- +18 more
Sep 23, 2022
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
-
Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)
Not yet recruiting
- Transfusion-dependent α-Thalassemia
- GMCN-508A Drug Product
- (no location specified)
Feb 24, 2023
ß-thalassemia Trial in Shanghai (BD211)
Not yet recruiting
- β-thalassemia
- BD211
-
Shanghai, ChinaShanghai Ruijin Hospital
Mar 16, 2023
Anemia Trial (Luspatercept)
Not yet recruiting
- Anemia
- Luspatercept
- (no location specified)
May 26, 2023
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen University General Hospital
May 8, 2023
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in
Recruiting
- Non-transfusion-dependent Thalassemia
- +2 more
- SLN124
- Placebo
-
Düsseldorf, Germany
- +19 more
Mar 18, 2022
a-thalassemia Trial in Nanning (a-globin restored autologous hematopoietic stem cells)
Recruiting
- α-thalassemia
- α-globin restored autologous hematopoietic stem cells
-
Nanning, Guangxi, ChinaPLA Joint Logistic Support Force No. 923 Hospital
May 6, 2023
Thalassemia Trial in Peshawar (Thalidomide and Hydroxyurea)
Completed
- Thalassemia
- Thalidomide and Hydroxyurea
-
Peshawar, Khyber Pakhtukhwa, PakistanBlood Diseases Clinic
Mar 10, 2022
Transfusion Dependent Beta-Thalassemia Trial in Nanning (GMCN-508B (LentiRed))
Recruiting
- Transfusion Dependent Beta-Thalassemia
- GMCN-508B (LentiRed)
-
Nanning, Guangxi, ChinaThe affiliated hospital of guangxi medical university
Feb 28, 2023
Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)
Not yet recruiting
- Thalassemia, Beta
- Thalassemia Major
- VGB-Ex01
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Sep 11, 2023
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)
Recruiting
- Transfusion Dependent Beta-Thalassaemia
- ET-01
-
Nanning, Guangxi, ChinaPLA 923 Hospital
Mar 2, 2023
Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)
Recruiting
- Thalassemia Major
- Transfusion-dependent Anemia
- Luspatercept Injectable Product
-
Guangzhou, Guangdong, ChinaThe second affiliated hospital of Sun Yat-sen University
Jul 15, 2022