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Non-transfusion dependent thalassemia

Showing 1 - 25 of >10,000

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Thalassemia Trial in Canada, United Kingdom, United States (AG-348)

Active, not recruiting
  • Thalassemia
  • Oakland, California
  • +3 more
Jan 26, 2023

Transfusion-dependent Thalassemia, Non-transfusion-dependent Thalassemia Trial in Worldwide (Deferasirox dispersable tablet

Completed
  • Transfusion-dependent Thalassemia
  • Non-transfusion-dependent Thalassemia
  • Deferasirox dispersable tablet (DT)
  • Deferasirox film coated tablet (FCT)
  • Alexandria, Egypt
  • +16 more
Sep 6, 2021

Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))

Active, not recruiting
  • Thalassemia
  • Los Angeles, California
  • +16 more
Aug 16, 2022

Transfusion-dependent Beta-thalassemia After Gene Therapy

Recruiting
  • Transfusion-dependent Beta-Thalassemia
  • Gene Therapy
  • Gene therapy
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Aug 6, 2023

Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)

Recruiting
  • Transfusion-dependent Thalassemia
  • Thalidomide Capsules
  • Placebo
  • Dhaka, Bangladesh
    Bangabandhu Sheikh Mujib Medical University
Oct 18, 2023

Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)

Active, not recruiting
  • Beta Thalassemia Intermedia
  • Camperdown, New South Wales, Australia
  • +18 more
Sep 23, 2022

Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

Completed
  • Transfusion-dependent Beta-Thalassemia
  • Peshawar, Khyber Pakhtunkhwa, Pakistan
    Blood Care Clinic
Nov 19, 2023

Beta Thalassemia Major Anemia Trial (SP-420)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • (no location specified)
Jan 20, 2023

Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

Not yet recruiting
  • Transfusion-dependent Beta-Thalassemia
  • KL003 cell injection Drug Product
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
May 8, 2023

ß-thalassemia Trial (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • (no location specified)
Mar 15, 2023

Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)

Not yet recruiting
  • Transfusion-dependent α-Thalassemia
  • GMCN-508A Drug Product
  • (no location specified)
Feb 24, 2023

ß-thalassemia Trial in Shanghai (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • Shanghai, China
    Shanghai Ruijin Hospital
Mar 16, 2023

Anemia Trial (Luspatercept)

Not yet recruiting
  • Anemia
  • Luspatercept
  • (no location specified)
May 26, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen University General Hospital
May 8, 2023

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in

Recruiting
  • Non-transfusion-dependent Thalassemia
  • +2 more
  • Düsseldorf, Germany
  • +19 more
Mar 18, 2022

a-thalassemia Trial in Nanning (a-globin restored autologous hematopoietic stem cells)

Recruiting
  • α-thalassemia
  • α-globin restored autologous hematopoietic stem cells
  • Nanning, Guangxi, China
    PLA Joint Logistic Support Force No. 923 Hospital
May 6, 2023

Thalassemia Trial in Peshawar (Thalidomide and Hydroxyurea)

Completed
  • Thalassemia
  • Thalidomide and Hydroxyurea
  • Peshawar, Khyber Pakhtukhwa, Pakistan
    Blood Diseases Clinic
Mar 10, 2022

ß-thalassemia, Ineffective Erythropoiesis, Chronic Anemia Trial in Worldwide (PTG-300)

Completed
  • β-thalassemia
  • +2 more
  • Oakland, California
  • +32 more
Jul 13, 2021

Transfusion Dependent Beta-Thalassemia Trial in Nanning (GMCN-508B (LentiRed))

Recruiting
  • Transfusion Dependent Beta-Thalassemia
  • GMCN-508B (LentiRed)
  • Nanning, Guangxi, China
    The affiliated hospital of guangxi medical university
Feb 28, 2023

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

Recruiting
  • Transfusion Dependent Beta Thalassemia
  • +3 more
  • EDIT-301
  • Oakland, California
  • +3 more
Jan 3, 2023

Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)

Recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Nanning, Guangxi, China
    PLA 923 Hospital
Mar 2, 2023

Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

Recruiting
  • Thalassemia Major
  • Transfusion-dependent Anemia
  • Luspatercept Injectable Product
  • Guangzhou, Guangdong, China
    The second affiliated hospital of Sun Yat-sen University
Jul 15, 2022

Beta-Thalassemia Trial in China (BRL-101)

Recruiting
  • Beta-Thalassemia
  • Guangzhou, Guangdong, China
  • +3 more
Nov 7, 2022

After Ex-vivo Gene Therapy With BIVV003 in Severe Sickle Cell

Recruiting
  • Blood and Lymphatic Diseases
  • Detroit, Michigan
    Investigational Site Number :8400001
Jul 6, 2022